Complete title: A Pilot Feasibility Study of Gene Transfer for X-Linked Severe Combined Immunodeficiency in Newly Diagnosed Infants Using a Self-Inactivating Lentiviral Vector to Transduce Autologous CD34+ Hematopoietic Cells
Research Study Number | 9356 |
Principal Investigator | Aleksandra Petrovic |
Phase | Pilot |
Other eligibility criteria may apply.
Research Study Number | 9356 |
Contact | Aleksandra Petrovic |
Keywords: Immunodeficiency Syndromes; Pediatric Cancers, Miscellaneous; Severe Combined Immunodeficiency Syndrome (SCID); Immune System Diseases; Genetic Diseases, Inborn; Genetic Diseases, X-Linked; DNA Repair-Deficiency Disorders; Infant, Newborn, Diseases; Metabolic Diseases; X-Linked Combined Immunodeficiency Diseases
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